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Barth syndrome -
September 19
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September 20, 2025 at 06:52
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Elamipretide
Cited Sources (Sep 19, 2025)
Stealth BioTherapeutics Announces FDA Accelerated Approval of Forzinity (elamipretide HCl), the First Therapy for Progressive and Life-limiting Ultra-rare Genetic Disease Barth Syndrome
prnewswire.com
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